Columnist Shalom Lim and his girlfriend, Amanda, were among the disability advocates who let their voices be heard at a ...

Avidity's exon-skipping therapy del-zota led to functional gains for people with DMD, regardless of their walking abilities, ...

For boys who start corticosteroids for DMD, being taller is tied with slower growth, and being older is tied to more weight ...

Satellos Bioscience is planning a Phase 2 trial in the U.S. to test SAT-3247 in children with Duchenne who are able to walk.

Adaptive clothing for Duchenne muscular dystrophy offers comfort, ease, and independence for those with muscle weakness and ...

The FDA has granted orphan drug designation to CRD-003, an investigational gene therapy for limb-girdle muscular dystrophy ...

Mondays are usually a relaxing day for columnist Betty Vertin, but this one left her flat on her back after lifting her son into the shower.

In recognition of Duchenne Muscular Dystrophy Awareness Month in September, the Duchenne Muscular Dystrophy Community Spotlight campaign features a series of stories highlighting the real-life ...

In recognition of Duchenne Muscular Dystrophy Awareness Month in September, the Duchenne Muscular Dystrophy Community Spotlight campaign features a series of stories highlighting the real-life ...

Yeah, when you’re having a caregiver or individual helping you out, overstepping and you want to set boundaries, the best way to communicate that is really just to communicate it — to tell them in ...

The U.S. Food and Drug Administration (FDA) has granted orphan drug status to NS-051/NCNP-04, an exon-skipping therapy ...

Doctors can use several tests to diagnose muscular dystrophy (MD). A correct diagnosis gives patients an understanding of how their disease is likely to progress. It also helps doctors do a better job ...