Pfizer shelves haemophilia gene therapy Beqvez

In a major breakthrough, four children born with severe visual impairments have experienced life-changing improvements in their ...
12 years after going public, beleaguered gene therapy company bluebird bio will be sold to private equity groups Carlyle and ...
Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...
Sensorion's Audiogene Phase I/II trial of the SENS-501 gene therapy programme has received a favourable recommendation from ...
Revolutionary gene therapy approaches show promise in treating various retinal conditions, potentially transforming treatment ...
MeiraGTx’s investigational gene therapy AAV-AIPL1 has improved the sight of 11 children who were born blind. MeiraGTx is ...
Latus Bio, Inc. (Latus), a biotechnology company pioneering advances in AAV gene therapy, is pleased to announce data ...
Bluebird Bio will sell itself to private equity firms Carlyle and SK Capital for about $30 million, the company said Friday.
A Connecticut boy is among four children all born with severe childhood blindness who gained “life-changing improvements” to ...
At the Envision Summit 2025 in San Juan, Puerto Rico, Mike Farkas, MD, discussed gene therapy research for retinal ...
By Sneha S K (Reuters) -Gene therapy maker bluebird bio on Friday agreed to be taken private by Carlyle Group and SK Capital ...