Sarepta prepares to present new data on Duchenne and limb-girdle muscular dystrophy gene therapy programs this week.
Rare Therapeutics will specifically advance gene therapies for extremely rare diseases with a goal of making them accessible globally.
The gene therapy market size is calculated at USD 11.4 billion in 2025 and is expected to reach around USD 58.87 billion by 2034, growing at a CAGR of 20% for the forecasted period.Ottawa, Oct. 08, ...
The country’s top drugmakers are set to meet in early December at the Four Seasons hotel in Georgetown with Donald Trump Jr.
In a setback for Sarepta Therapeutics, a New York panel has voted unanimously to recommend the state Medicaid program pause ...
Shares of Sarepta Therapeutics rose nearly 5% in early premarket trading on Wednesday as the company prepared to present new ...
Enzyme Replacement Therapy (ERT) generated over US$ 46 billion in 2024, driven by established treatments for Gaucher disease, ...