Discovery of the first molecular mechanism of action for a small molecule that improves RNA splicing in cells could lead to new therapeutics for the genetic disorder spinal muscular atrophy (SMA) and ...
Scientific insights often reflect a shift in perspective. For Envisagenics and its partners, insights may be gained through a more encompassing view of gene expression errors. This view includes ...
Splicing of SMN2 generally skips exon 7, resulting in the production of a truncated and inactivated form of the SMN protein. NVS-SM1, a new compound reported by Palacino and colleagues, facilitates ...
It's understood that degenerative diseases like Alzheimers and cancer can make a person's “golden years” look pretty bleak. However, there’s some hope on the horizon thanks to some new research from ...
A compound already used to treat pneumonia could become a new therapy for an inherited muscular wasting disease, according to researchers at the University of Oregon and the University of Rochester ...
PITTSBURGH, Pa., Dec. 16, 2020 (GLOBE NEWSWIRE) -- NeuBase Therapeutics, Inc. (Nasdaq: NBSE) ("NeuBase" or the "Company"), a biotechnology company accelerating the genetic revolution using a new class ...
Panorama Medicine is an RNA genomics- and computing-powered drug discovery company that develops therapeutic interventions for a range of common and rare diseases caused by messenger RNA (mRNA) ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback